Tackling Ponto-Cerebellar Hypoplasia 6 due to mitochondrial RARS2 defect in patients’ derived stem cells: from disease mechanism of tissue-specificity to novel experimental therapies

Responsabile scientifico: prof.ssa Garone Caterina

Ente finanziatore: MUR

Durata: 28/09/2023 - 27/09/2025